10 Recruiting Rare Diseases Clinical Trials
Explore open interventional and observational research studies actively enrolling participants across the USA. Verify eligibility and contact site coordinators directly.
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Top Recruiting Rare Diseases Studies
🟢 Recruiting Observational / Diagnostic 📋 Clinical Research Protocol
Genetic Study to Determine the Cause of Birth Defects in Newborns in Texas
📍 Baylor College of Medicine — Houston, Texas
View Study & Checklist ➔ 🟢 Recruiting Interventional Protocol 📊 Observational Clinical Research
A Multi-Site Leukopak Repository Providing Annotated Biospecimens for Approved Investigator-Directed Biomedical Research Initiatives
📍 Sanguine Biosciences — Waltham, Massachusetts
View Study & Checklist ➔ 🟢 Recruiting Interventional Protocol 📊 Observational Clinical Research
UW Undiagnosed Genetic Diseases Program
📍 University of Wisconsin School of Medicine and Public Health — Madison, Wisconsin
View Study & Checklist ➔ 🟢 Recruiting Interventional Protocol 📊 Observational Clinical Research
Baker Gordon Syndrome Natural History Study
📍 University of Missouri Columbia — Columbia, Missouri
View Study & Checklist ➔